Therapeutic Updates: Making Sense of Antisense and Other Advancements in Precision Therapies (Spanish)

Description: An update on recent developments and potential future avenues for genetic therapies across a variety of dominantly inherited illnesses
Runtime: 00:20:21

Speaker: Tim Miller, MD, PhD
Speaker title: ALS Center Co-Director
Speaker organization: Washington University in St. Louis

Event: 2019 DIAD Family Conference: Mutation, Participation, Innovation
Location: Los Angeles, California, USA
Year: 2019

Search tags: antisense oligonucleotides, precision therapies, genetic-focused therapies, APP, tau tangles, APOE4, Trem2, RNA, RNaseH, mRNA, siRNA, tau ASOs, CRISPR, clinical trials, data sharing, intrathecal infusion